Xu, Richard Huan; Rencz, Fanni; Sun, Ruiqi; Dong, Dong; … - 2025
Objective: Our objective was to develop and assess the psychometric properties of relevant bolt-on items for the EQ-5D-5L in patients with rare diseases (RDs). Methods: Nineteen new EQ-5D-5L bolt-ons were developed based on literature review, expert input and qualitative interviews and focus...